Please note that events are listed for Central Time Zone (Chicago). Upcoming Events May 26 1:00 pm - 2:00 pm Caregivers Support Group Jun 16 12:00 pm - 1:00 pm Caregivers Support Group: Father’s Day Group Jul 23 All day ADLD Center: 2nd International Symposium on ADLD Jul 26 July 26 - July 29 Cure LBSL: Patient & Scientific Conference Jul 28 1:00 pm - 2:00 pm Caregivers Support Group View Calendar Recent Posts Calyx: New Clinical Trial in cALD PMD Interview Study Opportunity Recruiting Now In Memorial and Honor – March 2024 Orchard Therapeutics Outlines U.S. Launch Plans for Lenmeldy™ (atidarsagene autotemcel), the Only Approved Therapy for Children with Early-onset Metachromatic Leukodystrophy FDA Approves First Gene Therapy for Children with Metachromatic Leukodystrophy In Memorial and Honor – February 2024 Two ALSP Studies Now Recruiting In Memorial and Honor – January 2024 Forge Biologics Announces Positive FBX-101 Clinical Trial Update in Patients with Krabbe Disease Identified by Newborn Screening Ahead of RUSP Vote In Memorial and Honor – December 2023 Read More News Share your story Read Stories